McIntosh, Jenny <br/><br/>
Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant.  [electronic resource] 

 -  Blood  Apr 2013 
 - 3335-44 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1528-0020 
<br/><br/><label>Standard No.: </label>10.1182/blood-2012-10-462200  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Blotting, Western<br/>Dependovirus--genetics<br/>Factor VIII--genetics<br/>Genetic Therapy<br/>Genetic Variation--genetics<br/>Genetic Vectors--administration & dosage<br/>Glycosylation<br/>Hemophilia A--genetics<br/>Humans<br/>Immune Tolerance<br/>Liver--metabolism<br/>Macaca mulatta<br/>Male<br/>Mice<br/>Mice, Inbred C57BL<br/>Mice, Knockout<br/>Peptide Fragments--genetics<br/>Promoter Regions, Genetic--genetics