TY - GEN AU - Cideciyan,Artur V AU - Jacobson,Samuel G AU - Beltran,William A AU - Sumaroka,Alexander AU - Swider,Malgorzata AU - Iwabe,Simone AU - Roman,Alejandro J AU - Olivares,Melani B AU - Schwartz,Sharon B AU - Komáromy,András M AU - Hauswirth,William W AU - Aguirre,Gustavo D TI - Human retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement SN - 1091-6490 PY - 2013///0409 KW - Adolescent KW - Adult KW - Animals KW - Child KW - Child, Preschool KW - Disease Models, Animal KW - Dogs KW - Genetic Therapy KW - Humans KW - Leber Congenital Amaurosis KW - genetics KW - Mutation KW - Photoreceptor Cells, Vertebrate KW - pathology KW - Retinal Degeneration KW - Time Factors KW - Vision, Ocular KW - Young Adult KW - cis-trans-Isomerases N1 - Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't UR - https://doi.org/10.1073/pnas.1218933110 ER -