Cideciyan, Artur V <br/><br/>
Human retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement.  [electronic resource] 

 -  Proceedings of the National Academy of Sciences of the United States of America  Feb 2013 
 - E517-25 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1091-6490 
<br/><br/><label>Standard No.: </label>10.1073/pnas.1218933110  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Adolescent<br/>Adult<br/>Animals<br/>Child<br/>Child, Preschool<br/>Disease Models, Animal<br/>Dogs<br/>Genetic Therapy<br/>Humans<br/>Leber Congenital Amaurosis--genetics<br/>Mutation<br/>Photoreceptor Cells, Vertebrate--pathology<br/>Retinal Degeneration--genetics<br/>Time Factors<br/>Vision, Ocular<br/>Young Adult<br/>cis-trans-Isomerases--genetics