Corti, Stefania <br/><br/>
Genetic correction of human induced pluripotent stem cells from patients with spinal muscular atrophy.  [electronic resource] 

 -  Science translational medicine  Dec 2012 
 - 165ra162 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1946-6242 
<br/><br/><label>Standard No.: </label>10.1126/scitranslmed.3004108  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Cell Transplantation<br/>Gene Expression<br/>Genetic Therapy<br/>Genetic Vectors<br/>Humans<br/>Motor Neurons--metabolism<br/>Muscular Atrophy, Spinal--genetics<br/>Pluripotent Stem Cells--cytology<br/>RNA Splicing<br/>Survival of Motor Neuron 1 Protein--genetics