Parenti, Giancarlo <br/><br/>
New strategies for the treatment of lysosomal storage diseases (review).  [electronic resource] 

 -  International journal of molecular medicine  Jan 2013 
 - 11-20 p.  digital 
<br/><br/> Publication Type: Journal Article; Review 
<br/><br/><label>ISSN: </label>1791-244X 
<br/><br/><label>Standard No.: </label>10.3892/ijmm.2012.1187  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Disease Models, Animal<br/>Enzyme Replacement Therapy--methods<br/>Genetic Therapy--methods<br/>Hematopoietic Stem Cell Transplantation--methods<br/>Humans<br/>Hydrolases--metabolism<br/>Lysosomal Storage Diseases--genetics<br/>Lysosomes--metabolism<br/>Molecular Chaperones--metabolism<br/>Proteostasis Deficiencies--therapy