Lee, Andrew J-H

Limited phenotypic effects of selectively augmenting the SMN protein in the neurons of a mouse model of severe spinal muscular atrophy. [electronic resource] - PloS one 2012 - e46353 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S.

1932-6203

10.1371/journal.pone.0046353 doi


Animals
Cellular Microenvironment
Disease Models, Animal
Female
Genetic Therapy
Humans
Male
Mice
Mice, Transgenic
Motor Activity
Motor Neurons--metabolism
Muscular Atrophy, Spinal--genetics
Neuromuscular Junction--genetics
Organ Specificity
Phenotype
Severity of Illness Index
Survival Rate
Survival of Motor Neuron 1 Protein--genetics
Synapses--genetics
Transgenes