TY - GEN AU - Rigo,Frank AU - Hua,Yimin AU - Krainer,Adrian R AU - Bennett,C Frank TI - Antisense-based therapy for the treatment of spinal muscular atrophy SN - 1540-8140 PY - 2013///0208 KW - Animals KW - Humans KW - Mice KW - Mice, Transgenic KW - Muscular Atrophy, Spinal KW - drug therapy KW - Oligonucleotides, Antisense KW - pharmacology KW - RNA, Messenger KW - drug effects KW - Survival of Motor Neuron 1 Protein KW - antagonists & inhibitors KW - Survival of Motor Neuron 2 Protein N1 - Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't UR - https://doi.org/10.1083/jcb.201207087 ER -