Rigo, Frank

Antisense-based therapy for the treatment of spinal muscular atrophy. [electronic resource] - The Journal of cell biology Oct 2012 - 21-5 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

1540-8140

10.1083/jcb.201207087 doi


Animals
Humans
Mice
Mice, Transgenic
Muscular Atrophy, Spinal--drug therapy
Oligonucleotides, Antisense--pharmacology
RNA, Messenger--drug effects
Survival of Motor Neuron 1 Protein--antagonists & inhibitors
Survival of Motor Neuron 2 Protein--antagonists & inhibitors