van Til, Niek P <br/><br/>
Correction of murine Rag2 severe combined immunodeficiency by lentiviral gene therapy using a codon-optimized RAG2 therapeutic transgene.  [electronic resource] 

 -  Molecular therapy : the journal of the American Society of Gene Therapy  Oct 2012 
 - 1968-80 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1525-0024 
<br/><br/><label>Standard No.: </label>10.1038/mt.2012.110  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>B-Lymphocytes--metabolism<br/>Cell Proliferation<br/>Chimerism<br/>Chromatin<br/>Codon--genetics<br/>DNA-Binding Proteins--genetics<br/>Female<br/>Gene Dosage<br/>Gene Rearrangement<br/>Genes, T-Cell Receptor beta<br/>Genetic Therapy--methods<br/>Genetic Vectors--genetics<br/>Hematopoietic Stem Cells--metabolism<br/>Lentivirus--genetics<br/>Male<br/>Mice<br/>Mice, Inbred BALB C<br/>Mice, Knockout<br/>Mice, SCID<br/>Phenotype<br/>Plasmids<br/>Promoter Regions, Genetic<br/>Sequence Analysis, DNA<br/>Severe Combined Immunodeficiency--genetics<br/>Spleen--cytology<br/>Spleen Focus-Forming Viruses--genetics<br/>T-Lymphocytes--metabolism<br/>Transduction, Genetic<br/>Transgenes