Suppression of premature termination codons as a therapeutic approach. [electronic resource]
- Critical reviews in biochemistry and molecular biology Sep 2012
- 444-63 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Review
1549-7798
10.3109/10409238.2012.694846 doi
Aminoglycosides--therapeutic use Animals Clinical Trials as Topic Codon, Nonsense--genetics Cystic Fibrosis Transmembrane Conductance Regulator--genetics Genetic Diseases, Inborn--drug therapy Humans Mice Nonsense Mediated mRNA Decay Peptide Chain Termination, Translational Phenotype Protein Biosynthesis Protein Synthesis Inhibitors--therapeutic use