New motor outcome function measures in evaluation of late-onset Pompe disease before and after enzyme replacement therapy. [electronic resource]
- Muscle & nerve Jun 2012
- 831-4 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1097-4598
10.1002/mus.23340 doi
Adult Age of Onset Aged Disability Evaluation Enzyme Replacement Therapy Female Follow-Up Studies Gait--physiology Glycogen Storage Disease Type II--drug therapy Humans Male Middle Aged Motor Activity--physiology Outcome Assessment, Health Care Treatment Outcome Walking--physiology