TY  - GEN
AU  - Breda,Laura
AU  - Casu,Carla
AU  - Gardenghi,Sara
AU  - Bianchi,Nicoletta
AU  - Cartegni,Luca
AU  - Narla,Mohandas
AU  - Yazdanbakhsh,Karina
AU  - Musso,Marco
AU  - Manwani,Deepa
AU  - Little,Jane
AU  - Gardner,Lawrence B
AU  - Kleinert,Dorothy A
AU  - Prus,Eugenia
AU  - Fibach,Eitan
AU  - Grady,Robert W
AU  - Giardina,Patricia J
AU  - Gambari,Roberto
AU  - Rivella,Stefano
TI  - Therapeutic hemoglobin levels after gene transfer in β-thalassemia mice and in hematopoietic cells of β-thalassemia and sickle cells disease patients
SN  - 1932-6203
PY  - 2012///0828
KW  - Adult
KW  - Anemia, Sickle Cell
KW  - blood
KW  - Animals
KW  - Ankyrins
KW  - genetics
KW  - Antigens, CD34
KW  - metabolism
KW  - Base Sequence
KW  - Cell Differentiation
KW  - Cell Line, Tumor
KW  - Cells, Cultured
KW  - Erythroid Precursor Cells
KW  - Gene Expression
KW  - Gene Transfer Techniques
KW  - Genetic Therapy
KW  - methods
KW  - Genetic Vectors
KW  - Hemoglobins
KW  - Humans
KW  - Insulator Elements
KW  - Lentivirus
KW  - Mice
KW  - Molecular Sequence Data
KW  - Mutation
KW  - NIH 3T3 Cells
KW  - beta-Globins
KW  - beta-Thalassemia
N1  - Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1371/journal.pone.0032345
ER  -