Synergistic effects of central nervous system-directed gene therapy and bone marrow transplantation in the murine model of infantile neuronal ceroid lipofuscinosis. [electronic resource]
- Annals of neurology Jun 2012
- 797-804 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1531-8249
10.1002/ana.23545 doi
Age Factors Animals Animals, Newborn Bone Marrow Transplantation--methods Brain--metabolism Dependovirus--genetics Disease Models, Animal Female Genetic Therapy--methods Genetic Vectors--administration & dosage Male Mice Mice, Knockout Motor Activity Neuronal Ceroid-Lipofuscinoses--pathology Rotarod Performance Test Thiolester Hydrolases--biosynthesis