Gene therapy rescues photoreceptor blindness in dogs and paves the way for treating human X-linked retinitis pigmentosa. [electronic resource]
- Proceedings of the National Academy of Sciences of the United States of America Feb 2012
- 2132-7 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
1091-6490
10.1073/pnas.1118847109 doi
Animals Blindness--genetics Dogs Eye Proteins--genetics Genetic Diseases, X-Linked--genetics Genetic Therapy Genotype Humans Mice Mutation--genetics Open Reading Frames--genetics Opsins--metabolism Phenotype Photoreceptor Cells, Vertebrate--pathology Protein Transport Retinal Bipolar Cells--pathology Retinitis Pigmentosa--genetics