Population pharmacokinetics and pharmacodynamics of cysteamine in nephropathic cystinosis patients. [electronic resource]
- Orphanet journal of rare diseases Dec 2011
- 86 p. digital
Publication Type: Clinical Trial; Journal Article
1750-1172
10.1186/1750-1172-6-86 doi
Adolescent Adult Body Weight Child Child, Preschool Cysteamine--administration & dosage Cystine--blood Cystinosis--drug therapy Dose-Response Relationship, Drug Fanconi Syndrome Female Humans Infant Male Nephrotic Syndrome--drug therapy Radiation-Protective Agents--administration & dosage Treatment Outcome Young Adult