Bouaita, Aicha

Downregulation of apoptosis-inducing factor in Harlequin mice induces progressive and severe optic atrophy which is durably prevented by AAV2-AIF1 gene therapy. [electronic resource] - Brain : a journal of neurology Jan 2012 - 35-52 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1460-2156

10.1093/brain/awr290 doi


Animals
Apoptosis Inducing Factor--genetics
Disease Models, Animal
Down-Regulation
Genetic Therapy
Mice
Optic Atrophy--genetics
Optic Nerve--metabolism
Retina--metabolism