TY  - GEN
AU  - Kang,Hyoung Jin
AU  - Bartholomae,Cynthia C
AU  - Paruzynski,Anna
AU  - Arens,Anne
AU  - Kim,Sujeong
AU  - Yu,Seung Shin
AU  - Hong,Youngtae
AU  - Joo,Chang-Wan
AU  - Yoon,Nam-Kyung
AU  - Rhim,Jung-Woo
AU  - Kim,Joong Gon
AU  - Von Kalle,Christof
AU  - Schmidt,Manfred
AU  - Kim,Sunyoung
AU  - Ahn,Hyo Seop
TI  - Retroviral gene therapy for X-linked chronic granulomatous disease: results from phase I/II trial
SN  - 1525-0024
PY  - 2012///0305
KW  - Adolescent
KW  - Child
KW  - Gene Expression Profiling
KW  - Genetic Therapy
KW  - Genetic Vectors
KW  - adverse effects
KW  - Granulomatous Disease, Chronic
KW  - therapy
KW  - Hematopoietic Stem Cell Transplantation
KW  - Hematopoietic Stem Cells
KW  - metabolism
KW  - Humans
KW  - Male
KW  - Membrane Glycoproteins
KW  - genetics
KW  - NADPH Oxidase 2
KW  - NADPH Oxidases
KW  - Retroviridae
KW  - Transduction, Genetic
KW  - Treatment Outcome
KW  - Virus Integration
N1  - Publication Type: Clinical Trial, Phase I; Clinical Trial, Phase II; Journal Article; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1038/mt.2011.166
ER  -