Kang, Hyoung Jin

Retroviral gene therapy for X-linked chronic granulomatous disease: results from phase I/II trial. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Nov 2011 - 2092-101 p. digital

Publication Type: Clinical Trial, Phase I; Clinical Trial, Phase II; Journal Article; Research Support, Non-U.S. Gov't

1525-0024

10.1038/mt.2011.166 doi


Adolescent
Child
Gene Expression Profiling
Genetic Therapy
Genetic Vectors--adverse effects
Granulomatous Disease, Chronic--therapy
Hematopoietic Stem Cell Transplantation--adverse effects
Hematopoietic Stem Cells--metabolism
Humans
Male
Membrane Glycoproteins--genetics
NADPH Oxidase 2
NADPH Oxidases--genetics
Retroviridae--genetics
Transduction, Genetic
Treatment Outcome
Virus Integration