Marucha, Jolanta

Improvement in the range of joint motion in seven patients with mucopolysaccharidosis type II during experimental gene expression-targeted isoflavone therapy (GET IT). [electronic resource] - American journal of medical genetics. Part A Sep 2011 - 2257-62 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1552-4833

10.1002/ajmg.a.34146 doi


Adolescent
Adult
Child
Connective Tissue--drug effects
Gene Expression--drug effects
Genistein--administration & dosage
Glycosaminoglycans--metabolism
Humans
Isoflavones--administration & dosage
Male
Molecular Targeted Therapy
Mucopolysaccharidosis II--drug therapy
Range of Motion, Articular--drug effects