Improvement in the range of joint motion in seven patients with mucopolysaccharidosis type II during experimental gene expression-targeted isoflavone therapy (GET IT). [electronic resource]
- American journal of medical genetics. Part A Sep 2011
- 2257-62 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1552-4833
10.1002/ajmg.a.34146 doi
Adolescent Adult Child Connective Tissue--drug effects Gene Expression--drug effects Genistein--administration & dosage Glycosaminoglycans--metabolism Humans Isoflavones--administration & dosage Male Molecular Targeted Therapy Mucopolysaccharidosis II--drug therapy Range of Motion, Articular--drug effects