Intrathecal tripeptidyl-peptidase 1 reduces lysosomal storage in a canine model of late infantile neuronal ceroid lipofuscinosis. [electronic resource]
- Molecular genetics and metabolism Nov 2011
- 325-37 p. digital
Publication Type: Journal Article
1096-7206
10.1016/j.ymgme.2011.06.018 doi
Aminopeptidases--administration & dosage Animals CHO Cells Central Nervous System--metabolism Chromatography, Gel Chromatography, Ion Exchange Cricetinae Cricetulus Dipeptidyl-Peptidases and Tripeptidyl-Peptidases--administration & dosage Dogs Electrophysiology Fluorescence Gene Knockout Techniques Humans Immunoassay Immunoglobulin E--blood Injections, Spinal Lysosomes--metabolism Magnetic Resonance Imaging Maze Learning--drug effects Neuronal Ceroid-Lipofuscinoses--drug therapy Recombinant Proteins--pharmacology Serine Proteases--administration & dosage Tripeptidyl-Peptidase 1