Baldo, Guilherme

Recombinant encapsulated cells overexpressing alpha-L-iduronidase correct enzyme deficiency in human mucopolysaccharidosis type I cells. [electronic resource] - Cells, tissues, organs 2012 - 323-9 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1422-6421

10.1159/000327532 doi


Animals
Capsules
Cell Line
Cell Proliferation
Cell Survival
Cells, Immobilized--metabolism
Coculture Techniques
Cricetinae
Cryopreservation
Fibroblasts--enzymology
Glycosaminoglycans--metabolism
Humans
Iduronidase--metabolism
Mucopolysaccharidosis I--enzymology
Receptor, IGF Type 2--metabolism
Recombination, Genetic--genetics