Zhang, Shiqiang

Rescue of ATP7B function in hepatocyte-like cells from Wilson's disease induced pluripotent stem cells using gene therapy or the chaperone drug curcumin. [electronic resource] - Human molecular genetics Aug 2011 - 3176-87 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1460-2083

10.1093/hmg/ddr223 doi


Adenosine Triphosphatases--genetics
Base Sequence
Cation Transport Proteins--genetics
Copper--metabolism
Copper-Transporting ATPases
Curcumin--therapeutic use
Genetic Therapy
Hepatocytes--metabolism
Hepatolenticular Degeneration--drug therapy
Humans
Induced Pluripotent Stem Cells--metabolism
Male
Middle Aged
Molecular Chaperones--therapeutic use
Molecular Sequence Data
Mutation--genetics
Protein Transport
Subcellular Fractions--metabolism