Butchbach, Matthew E R <br/><br/>
Trans-splicing, more than meets the eye: multifaceted therapeutics for spinal muscular atrophy.  [electronic resource] 

 -  Human gene therapy  Feb 2011 
 - 121-5 p.  digital 
<br/><br/> Publication Type: Comment; Journal Article 
<br/><br/><label>ISSN: </label>1557-7422 
<br/><br/><label>Standard No.: </label>10.1089/hum.2011.903  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Gene Expression<br/>Genetic Therapy<br/>Humans<br/>Insulin-Like Growth Factor I--metabolism<br/>Mice<br/>Mice, Transgenic<br/>Muscular Atrophy, Spinal--genetics<br/>Survival of Motor Neuron 1 Protein--genetics<br/>Survival of Motor Neuron 2 Protein--genetics<br/>Trans-Splicing