TY  - GEN
AU  - Nathwani,Amit C
AU  - Rosales,Cecilia
AU  - McIntosh,Jenny
AU  - Rastegarlari,Ghasem
AU  - Nathwani,Devhrut
AU  - Raj,Deepak
AU  - Nawathe,Sushmita
AU  - Waddington,Simon N
AU  - Bronson,Roderick
AU  - Jackson,Scott
AU  - Donahue,Robert E
AU  - High,Katherine A
AU  - Mingozzi,Federico
AU  - Ng,Catherine Y C
AU  - Zhou,Junfang
AU  - Spence,Yunyu
AU  - McCarville,M Beth
AU  - Valentine,Marc
AU  - Allay,James
AU  - Coleman,John
AU  - Sleep,Susan
AU  - Gray,John T
AU  - Nienhuis,Arthur W
AU  - Davidoff,Andrew M
TI  - Long-term safety and efficacy following systemic administration of a self-complementary AAV vector encoding human FIX pseudotyped with serotype 5 and 8 capsid proteins
SN  - 1525-0024
PY  - 2011///1102
KW  - Animals
KW  - Capsid Proteins
KW  - genetics
KW  - Dependovirus
KW  - Factor IX
KW  - Gene Expression
KW  - Genetic Therapy
KW  - methods
KW  - Genetic Vectors
KW  - HEK293 Cells
KW  - Hemophilia B
KW  - Humans
KW  - In Situ Hybridization, Fluorescence
KW  - Liver
KW  - metabolism
KW  - Macaca
KW  - Mice
N1  - Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1038/mt.2010.274
ER  -