Gentner, Bernhard <br/><br/>
Identification of hematopoietic stem cell-specific miRNAs enables gene therapy of globoid cell leukodystrophy.  [electronic resource] 

 -  Science translational medicine  Nov 2010 
 - 58ra84 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1946-6242 
<br/><br/><label>Standard No.: </label>10.1126/scitranslmed.3001522  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Cell Differentiation<br/>Cell Separation<br/>Cytoprotection<br/>Galactosylceramidase--metabolism<br/>Gene Expression Regulation<br/>Genes, Transgenic, Suicide<br/>Genetic Therapy<br/>Hematopoietic Stem Cells--cytology<br/>Humans<br/>Leukodystrophy, Globoid Cell--genetics<br/>Mice<br/>Mice, SCID<br/>MicroRNAs--genetics<br/>Organ Specificity--genetics