McNeer, Nicole A

Nanoparticles deliver triplex-forming PNAs for site-specific genomic recombination in CD34+ human hematopoietic progenitors. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Jan 2011 - 172-80 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural

1525-0024

10.1038/mt.2010.200 doi


Antigens, CD34--biosynthesis
Cell Survival--drug effects
Cells, Cultured
DNA--genetics
Gene Targeting--methods
Gene Transfer Techniques
Genome
Hematopoietic Stem Cells--cytology
Humans
Lactic Acid--pharmacology
Nanoparticles--administration & dosage
Oligonucleotides--pharmacology
Particle Size
Peptide Nucleic Acids--administration & dosage
Polyglycolic Acid--pharmacology
Polylactic Acid-Polyglycolic Acid Copolymer
Receptors, CCR5--genetics
Recombination, Genetic
Targeted Gene Repair
beta-Globins--genetics