TY  - GEN
AU  - van Capelle,C I
AU  - van der Beek,N A M E
AU  - Hagemans,M L C
AU  - Arts,W F M
AU  - Hop,W C J
AU  - Lee,P
AU  - Jaeken,J
AU  - Frohn-Mulder,I M E
AU  - Merkus,P J F M
AU  - Corzo,D
AU  - Puga,A C
AU  - Reuser,A J
AU  - van der Ploeg,A T
TI  - Effect of enzyme therapy in juvenile patients with Pompe disease: a three-year open-label study
SN  - 1873-2364
PY  - 2011///0307
KW  - Adolescent
KW  - Child
KW  - Child, Preschool
KW  - Enzyme Replacement Therapy
KW  - Female
KW  - Glucan 1,4-alpha-Glucosidase
KW  - therapeutic use
KW  - Glycogen Storage Disease Type II
KW  - physiopathology
KW  - Humans
KW  - Male
KW  - Muscle, Skeletal
KW  - Recombinant Proteins
KW  - Treatment Outcome
N1  - Publication Type: Clinical Trial, Phase II; Journal Article; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1016/j.nmd.2010.07.277
ER  -