TY  - GEN
AU  - Robert-Richard,Elodie
AU  - Lalanne,Magalie
AU  - Lamrissi-Garcia,Isabelle
AU  - Guyonnet-Duperat,Véronique
AU  - Richard,Emmanuel
AU  - Pitard,Vincent
AU  - Mazurier,Fréderic
AU  - Moreau-Gaudry,François
AU  - Ged,Cécile
AU  - de Verneuil,Hubert
TI  - Modeling of congenital erythropoietic porphyria by RNA interference: a new tool for preclinical gene therapy evaluation
SN  - 1521-2254
PY  - 2010///1223
KW  - Animals
KW  - Disease Models, Animal
KW  - Genetic Therapy
KW  - methods
KW  - Hematopoietic Stem Cells
KW  - metabolism
KW  - Humans
KW  - K562 Cells
KW  - Lentivirus
KW  - genetics
KW  - Mice
KW  - Porphyria, Erythropoietic
KW  - enzymology
KW  - RNA Interference
KW  - Uroporphyrinogen III Synthetase
N1  - Publication Type: Evaluation Study; Journal Article; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1002/jgm.1478
ER  -