Robert-Richard, Elodie <br/><br/>
Modeling of congenital erythropoietic porphyria by RNA interference: a new tool for preclinical gene therapy evaluation.  [electronic resource] 

 -  The journal of gene medicine  Aug 2010 
 - 637-46 p.  digital 
<br/><br/> Publication Type: Evaluation Study; Journal Article; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1521-2254 
<br/><br/><label>Standard No.: </label>10.1002/jgm.1478  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Disease Models, Animal<br/>Genetic Therapy--methods<br/>Hematopoietic Stem Cells--metabolism<br/>Humans<br/>K562 Cells<br/>Lentivirus--genetics<br/>Mice<br/>Porphyria, Erythropoietic--enzymology<br/>RNA Interference<br/>Uroporphyrinogen III Synthetase--genetics