TY  - GEN
AU  - Valori,Chiara F
AU  - Ning,Ke
AU  - Wyles,Matthew
AU  - Mead,Richard J
AU  - Grierson,Andrew J
AU  - Shaw,Pamela J
AU  - Azzouz,Mimoun
TI  - Systemic delivery of scAAV9 expressing SMN prolongs survival in a model of spinal muscular atrophy
SN  - 1946-6242
PY  - 2010///1012
KW  - Animals
KW  - Animals, Newborn
KW  - Base Sequence
KW  - Codon
KW  - genetics
KW  - Dependovirus
KW  - Disease Models, Animal
KW  - Fibroblasts
KW  - metabolism
KW  - Gene Transfer Techniques
KW  - Genetic Therapy
KW  - Mice
KW  - Molecular Sequence Data
KW  - Motor Activity
KW  - physiology
KW  - Muscular Atrophy, Spinal
KW  - Mutation
KW  - Phenotype
KW  - Survival Analysis
KW  - Survival of Motor Neuron 1 Protein
N1  - Publication Type: Journal Article
UR  - https://doi.org/10.1126/scitranslmed.3000830
ER  -