Valori, Chiara F <br/><br/>
Systemic delivery of scAAV9 expressing SMN prolongs survival in a model of spinal muscular atrophy.  [electronic resource] 

 -  Science translational medicine  Jun 2010 
 - 35ra42 p.  digital 
<br/><br/> Publication Type: Journal Article 
<br/><br/><label>ISSN: </label>1946-6242 
<br/><br/><label>Standard No.: </label>10.1126/scitranslmed.3000830  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Animals, Newborn<br/>Base Sequence<br/>Codon--genetics<br/>Dependovirus--genetics<br/>Disease Models, Animal<br/>Fibroblasts--metabolism<br/>Gene Transfer Techniques<br/>Genetic Therapy<br/>Mice<br/>Molecular Sequence Data<br/>Motor Activity--physiology<br/>Muscular Atrophy, Spinal--genetics<br/>Mutation--genetics<br/>Phenotype<br/>Survival Analysis<br/>Survival of Motor Neuron 1 Protein--genetics