Koppanati, B M

Improvement of the mdx mouse dystrophic phenotype by systemic in utero AAV8 delivery of a minidystrophin gene. [electronic resource] - Gene therapy Nov 2010 - 1355-62 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, U.S. Gov't, Non-P.H.S.

1476-5462

10.1038/gt.2010.84 doi


Animals
Cytomegalovirus--genetics
Dependovirus--genetics
Dystrophin--genetics
Genetic Therapy
Genetic Vectors--administration & dosage
Humans
Mice
Mice, Inbred C57BL
Mice, Inbred mdx
Muscular Dystrophy, Animal--genetics
Muscular Dystrophy, Duchenne--genetics
Phenotype
Promoter Regions, Genetic