Amado, Defne

Safety and efficacy of subretinal readministration of a viral vector in large animals to treat congenital blindness. [electronic resource] - Science translational medicine Mar 2010 - 21ra16 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

1946-6242

10.1126/scitranslmed.3000659 doi


Adult
Aged
Aged, 80 and over
Animals
Anterior Chamber--immunology
Antibodies, Neutralizing--immunology
Blindness--congenital
Capsid--immunology
Carrier Proteins--genetics
Dependovirus--genetics
Dogs
Drug Administration Routes
Eye Proteins--genetics
Genetic Therapy
Genetic Vectors--administration & dosage
Humans
Immunity--immunology
Immunohistochemistry
Middle Aged
Postmortem Changes
Primates
Retina--pathology
Titrimetry
Treatment Outcome
cis-trans-Isomerases