Tylki-Szymanska, Anna

Efficacy of recombinant human alpha-L-iduronidase (laronidase) on restricted range of motion of upper extremities in mucopolysaccharidosis type I patients. [electronic resource] - Journal of inherited metabolic disease Apr 2010 - 151-7 p. digital

Publication Type: Clinical Trial; Journal Article

1573-2665

10.1007/s10545-010-9059-9 doi


Activities of Daily Living
Adolescent
Adult
Arthrometry, Articular
Child
Child, Preschool
Disease Progression
Elbow Joint--drug effects
Enzyme Replacement Therapy--methods
Female
Humans
Iduronidase--therapeutic use
Infant
Male
Movement--drug effects
Mucopolysaccharidosis I--drug therapy
Range of Motion, Articular--drug effects
Recombinant Proteins--therapeutic use
Self Care
Shoulder Joint--drug effects
Wrist Joint--drug effects
Young Adult