Efficacy of recombinant human alpha-L-iduronidase (laronidase) on restricted range of motion of upper extremities in mucopolysaccharidosis type I patients. [electronic resource]
- Journal of inherited metabolic disease Apr 2010
- 151-7 p. digital
Publication Type: Clinical Trial; Journal Article
1573-2665
10.1007/s10545-010-9059-9 doi
Activities of Daily Living Adolescent Adult Arthrometry, Articular Child Child, Preschool Disease Progression Elbow Joint--drug effects Enzyme Replacement Therapy--methods Female Humans Iduronidase--therapeutic use Infant Male Movement--drug effects Mucopolysaccharidosis I--drug therapy Range of Motion, Articular--drug effects Recombinant Proteins--therapeutic use Self Care Shoulder Joint--drug effects Wrist Joint--drug effects Young Adult