TY  - GEN
AU  - Wraith,James E
AU  - Vecchio,Darleen
AU  - Jacklin,Elizabeth
AU  - Abel,Larry
AU  - Chadha-Boreham,Harbajan
AU  - Luzy,Cécile
AU  - Giorgino,Ruben
AU  - Patterson,Marc C
TI  - Miglustat in adult and juvenile patients with Niemann-Pick disease type C: long-term data from a clinical trial
SN  - 1096-7206
PY  - 2010///0712
KW  - 1-Deoxynojirimycin
KW  - adverse effects
KW  - Adolescent
KW  - Adult
KW  - Child
KW  - Deglutition
KW  - drug effects
KW  - Diarrhea
KW  - chemically induced
KW  - Female
KW  - Humans
KW  - Niemann-Pick Disease, Type C
KW  - drug therapy
KW  - Walking
KW  - Weight Loss
N1  - Publication Type: Clinical Trial; Journal Article; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1016/j.ymgme.2009.12.006
ER  -