Wraith, James E <br/><br/>
Miglustat in adult and juvenile patients with Niemann-Pick disease type C: long-term data from a clinical trial.  [electronic resource] 

 -  Molecular genetics and metabolism  Apr 2010 
 - 351-7 p.  digital 
<br/><br/> Publication Type: Clinical Trial; Journal Article; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1096-7206 
<br/><br/><label>Standard No.: </label>10.1016/j.ymgme.2009.12.006  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>1-Deoxynojirimycin--adverse effects<br/>Adolescent<br/>Adult<br/>Child<br/>Deglutition--drug effects<br/>Diarrhea--chemically induced<br/>Female<br/>Humans<br/>Niemann-Pick Disease, Type C--drug therapy<br/>Walking<br/>Weight Loss