Targeted correction of a thalassemia-associated beta-globin mutation induced by pseudo-complementary peptide nucleic acids. [electronic resource]
- Nucleic acids research Jun 2009
- 3635-44 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural
1362-4962
10.1093/nar/gkp217 doi
Animals CHO Cells Cell Line Cricetinae Cricetulus Gene Targeting--methods Humans Mutation Peptide Nucleic Acids--chemistry Plasmids--genetics Recombination, Genetic S Phase Thalassemia--genetics Xeroderma Pigmentosum Group A Protein--metabolism beta-Globins--genetics