Maguire, Katie

Genetic correction of splice site mutation in purified and enriched myoblasts isolated from mdx5cv mice. [electronic resource] - BMC molecular biology Feb 2009 - 15 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural

1471-2199

10.1186/1471-2199-10-15 doi


Animals
Cells, Cultured
Gene Knockdown Techniques
Male
Mice
Mice, Inbred mdx
Muscular Dystrophy, Duchenne--genetics
MutS Homolog 2 Protein--metabolism
Mutation--genetics
Myoblasts--cytology
RNA Interference
RNA Splice Sites--genetics
Targeted Gene Repair--methods