Rate of disease progression during long-term follow-up of patients with late-onset Pompe disease. [electronic resource]
- Neuromuscular disorders : NMD Feb 2009
- 113-7 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
0960-8966
10.1016/j.nmd.2008.11.007 doi
Activities of Daily Living Adult Age of Onset Aged Comorbidity Cost of Illness Disability Evaluation Disease Progression Female Follow-Up Studies Glycogen Storage Disease Type II--epidemiology Humans Male Middle Aged Monitoring, Physiologic--standards Muscle Weakness--epidemiology Muscle, Skeletal--physiopathology Respiratory Paralysis--epidemiology Time Factors Ventilators, Mechanical--statistics & numerical data Wheelchairs--statistics & numerical data