Meyer, Kathrin

Rescue of a severe mouse model for spinal muscular atrophy by U7 snRNA-mediated splicing modulation. [electronic resource] - Human molecular genetics Feb 2009 - 546-55 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1460-2083

10.1093/hmg/ddn382 doi


Animals
Base Sequence
Exons
Genetic Therapy
Humans
Mice
Mice, Transgenic
Molecular Sequence Data
Muscular Atrophy, Spinal--genetics
RNA Splicing
RNA, Small Nuclear--genetics
Survival of Motor Neuron 2 Protein--genetics