Metachromatic leukodystrophy: an overview of current and prospective treatments. [electronic resource]
- Bone marrow transplantation Oct 2008
- S2-6 p. digital
Publication Type: Journal Article; Review
1476-5365
10.1038/bmt.2008.275 doi
Blood-Brain Barrier--enzymology Cerebroside-Sulfatase--therapeutic use Clinical Trials, Phase I as Topic Clinical Trials, Phase II as Topic Genetic Therapy--trends Graft vs Host Disease Hematopoietic Stem Cell Transplantation--trends Humans Leukodystrophy, Metachromatic--enzymology Recombinant Proteins--therapeutic use Risk Factors Transplantation, Autologous Transplantation, Homologous