Correction of ADAMTS13 deficiency by in utero gene transfer of lentiviral vector encoding ADAMTS13 genes. [electronic resource]
- Molecular therapy : the journal of the American Society of Gene Therapy Jan 2009
- 34-41 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural
1525-0024
10.1038/mt.2008.223 doi
ADAM Proteins--deficiency ADAMTS13 Protein Animals Blotting, Western Female Genetic Therapy--methods Genetic Vectors--genetics Humans Immunoprecipitation Lentivirus--genetics Mice Mice, Mutant Strains Microscopy, Fluorescence Purpura, Thrombotic Thrombocytopenic--genetics Uterus