Detection of human survival motor neuron (SMN) protein in mice containing the SMN2 transgene: applicability to preclinical therapy development for spinal muscular atrophy. [electronic resource]
- Journal of neuroscience methods Oct 2008
- 36-43 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
0165-0270
10.1016/j.jneumeth.2008.07.024 doi
Alternative Splicing--genetics Amino Acid Sequence Animals Antibodies, Monoclonal--metabolism Cells, Cultured Disease Models, Animal Enzyme Inhibitors Epitope Mapping--methods Fibroblasts--drug effects Gene Expression Regulation--drug effects Humans Hydroxyurea--therapeutic use Indoles Mice Mice, Transgenic--metabolism Muscular Atrophy, Spinal--drug therapy SMN Complex Proteins--genetics Spinal Cord--drug effects Survival of Motor Neuron 2 Protein Valproic Acid--therapeutic use