Chang, Alex H

Erythroid-specific human factor IX delivery from in vivo selected hematopoietic stem cells following nonmyeloablative conditioning in hemophilia B mice. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Oct 2008 - 1745-52 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

1525-0024

10.1038/mt.2008.161 doi


Animals
DNA Modification Methylases--metabolism
DNA Repair Enzymes--metabolism
Factor IX--administration & dosage
Genetic Vectors
Hematopoietic Stem Cells--cytology
Hemophilia B--therapy
Homeostasis--drug effects
Humans
Lentivirus--genetics
Mice
Mice, Inbred C57BL
Recombinant Proteins--administration & dosage
Tumor Suppressor Proteins--metabolism