Brunetti-Pierri, Nicola

Phenotypic correction of ornithine transcarbamylase deficiency using low dose helper-dependent adenoviral vectors. [electronic resource] - The journal of gene medicine Aug 2008 - 890-6 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural

1521-2254

10.1002/jgm.1218 doi


Adenoviridae--genetics
Amino Acid Metabolism, Inborn Errors--genetics
Animals
Disease Models, Animal
Genetic Therapy--methods
Genetic Vectors
Helper Viruses--genetics
Histocytochemistry
Liver--metabolism
Mice
Mice, Mutant Strains
Ornithine Carbamoyltransferase--genetics
Ornithine Carbamoyltransferase Deficiency Disease
Orotic Acid--urine
Transgenes