TY  - GEN
AU  - van Capelle,C I
AU  - Winkel,L P F
AU  - Hagemans,M L C
AU  - Shapira,S K
AU  - Arts,W F M
AU  - van Doorn,P A
AU  - Hop,W C J
AU  - Reuser,A J J
AU  - van der Ploeg,A T
TI  - Eight years experience with enzyme replacement therapy in two children and one adult with Pompe disease
SN  - 0960-8966
PY  - 2008///0924
KW  - Adolescent
KW  - Adult
KW  - Animals
KW  - CHO Cells
KW  - drug effects
KW  - Child
KW  - Cricetinae
KW  - Cricetulus
KW  - Female
KW  - Glycogen Storage Disease Type II
KW  - drug therapy
KW  - Humans
KW  - Longitudinal Studies
KW  - Male
KW  - Muscle, Skeletal
KW  - Treatment Outcome
KW  - alpha-Glucosidases
KW  - therapeutic use
N1  - Publication Type: Case Reports; Journal Article; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1016/j.nmd.2008.04.009
ER  -