Fabry disease--whom to treat and when. [electronic resource]
- Clinical therapeutics 2008
- S43-4 p. digital
Publication Type: Journal Article
0149-2918
10.1016/s0149-2918(08)80037-9 doi
Adolescent Adult Child Cost of Illness Fabry Disease--complications Family Humans Isoenzymes--therapeutic use Mutation, Missense--genetics alpha-Galactosidase--therapeutic use