Mehta, Atul

Gaucher disease: unmet treatment needs. [electronic resource] - Acta paediatrica (Oslo, Norway : 1992) Apr 2008 - 83-7 p. digital

Publication Type: Journal Article; Review

1651-2227

10.1111/j.1651-2227.2008.00653.x doi


1-Deoxynojirimycin--analogs & derivatives
Enzyme Inhibitors--therapeutic use
Gaucher Disease--complications
Glucosylceramidase--therapeutic use
Glycoside Hydrolase Inhibitors
Health Services Accessibility
Hematologic Neoplasms--etiology
Humans
Knee Joint--pathology
Magnetic Resonance Imaging
Recombinant Proteins--therapeutic use