Robert-Richard, Elodie

Effective gene therapy of mice with congenital erythropoietic porphyria is facilitated by a survival advantage of corrected erythroid cells. [electronic resource] - American journal of human genetics Jan 2008 - 113-24 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1537-6605

10.1016/j.ajhg.2007.09.007 doi


Animals
Cell Survival
Disease Models, Animal
Erythrocytes
Female
Genetic Therapy
Genetic Vectors
Hematopoietic Stem Cells
Lentivirus
Male
Mice
Mice, Inbred BALB C
Porphyria, Erythropoietic--genetics
Uroporphyrinogen III Synthetase--genetics