Patterson, Marc C <br/><br/>
Miglustat for treatment of Niemann-Pick C disease: a randomised controlled study.  [electronic resource] 

 -  The Lancet. Neurology  Sep 2007 
 - 765-72 p.  digital 
<br/><br/> Publication Type: Clinical Trial; Journal Article; Randomized Controlled Trial; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1474-4422 
<br/><br/><label>Standard No.: </label>10.1016/S1474-4422(07)70194-1  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>1-Deoxynojirimycin--analogs & derivatives<br/>Adolescent<br/>Adult<br/>Age Factors<br/>Analysis of Variance<br/>Child<br/>Child, Preschool<br/>Cohort Studies<br/>Deglutition--drug effects<br/>Double-Blind Method<br/>Drug Administration Schedule<br/>Enzyme Inhibitors--therapeutic use<br/>Female<br/>Humans<br/>Male<br/>Niemann-Pick Disease, Type C--drug therapy<br/>Retrospective Studies<br/>Saccades--drug effects<br/>Severity of Illness Index